Journal article
Treatment with Ataluren for Duchene Muscular Dystrophy
Pediatric neurology briefs, v 34, pp 12-12
04 Dec 2020
PMID: 33304086
Abstract
Investigators from Europe and the USA, representing the STRIDE Registry and
Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural
History Study (DNHS), examined the effectiveness of ataluren and standard of
care in the Registry versus stand of care alone in the CINRG DNHS.
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Details
- Title
- Treatment with Ataluren for Duchene Muscular Dystrophy
- Creators
- Sameh S. Morkous - Lehigh Valley Hospital-Pocono
- Publication Details
- Pediatric neurology briefs, v 34, pp 12-12
- Publisher
- Pediatric Neurology Briefs Publishers
- Number of pages
- 1
- Resource Type
- Journal article
- Language
- English
- Academic Unit
- Pediatrics
- Other Identifier
- 991022065041704721